PTC Therapeutics, Inc.

Pharmaceutical & medical device company payment data from CMS Open Payments.

Total Payments
$56.6M
Doctors Paid
1,083
Transactions
9,790
2024 Total
$8.4M

Payment Breakdown by Category

Research$49.2M (87.0%)
Consulting$2.8M (4.9%)
Royalty/License$482,303 (0.9%)
Travel$294,283 (0.5%)
Food & Beverage$98,485 (0.2%)

Payments by Nature

Nature of Payment Amount Transactions Share
Unspecified $49.2M 5,286 87.0%
Compensation for services other than consulting, including serving as faculty or as a speaker at a venue other than a continuing education program $3.5M 340 6.3%
Consulting Fee $2.8M 697 4.9%
Royalty or License $482,303 20 0.9%
Travel and Lodging $294,283 605 0.5%
Food and Beverage $98,485 2,433 0.2%
Space rental or facility fees (teaching hospital only) $71,845 42 0.1%
Education $54,467 356 0.1%
Grant $11,675 8 0.0%
Charitable Contribution $7,000 3 0.0%

Payments by Type

Research
$49.2M
5,286 transactions
General
$7.3M
4,504 transactions

Research Studies & Clinical Trials

Study Name Total Paid Doctors Records
A PHASE 2/3 STUDY TO EVALUATE THE EFFICACY AND SAFETY OF UNESBULIN IN UNRESECTABLE OR METASTATIC, RELAPSED OR REFRACTORY LEIOMYOSARCOMA $6.9M 9 556
AN OPEN-LABEL, SAFETY STUDY FOR ATALUREN (PTC124) PATIENTS WITH NONSENSE MUTATION DYSTROPHINOPATHY $2.5M 0 794
AN OPEN-LABEL TRIAL TO ADDRESS THE SAFETY OF THE SMARTFLOW MR-COMPATIBLE VENTRICULAR CANNULA FOR ADMINISTERING ELADOCAGENE EXUPARVOVEC TO PEDIATRIC SUBJECTS $2.4M 3 98
TQT STUDY - PHASE 1 PLACEBO AND POSITIVE CONTROLLED STUDY TO ASSESS THE EFFECT OF SINGLE THERAPEUTIC (400 MG) AND SUPRATHERAPEUTIC VATIQUINONE (1200 MG) DOSES ON QTCF PROLONGATION BY USING CONCENTRATION-EFFECT MODELLING (CEM) $2.1M 0 18
EFFICACY AND SAFETY STUDY OF VATIQUINONE FOR THE TREATMENT OF MITOCHONDRIAL DISEASE SUBJECTS WITH REFRACTORY EPILEPSY $2.0M 2 463
A PHASE 3, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED EFFICACY AND SAFETY STUDY OF ATALUREN IN PATIENTS WITH NONSENSE MUTATION DUCHENNE MUSCULAR DYSTROPHY AND OPEN-LABEL EXTENSION $1.8M 0 450
A PHASE IB STUDY OF PTC596 IN CHILDREN WITH NEWLY DIAGNOSED DIFFUSE INTRINSIC PONTINE GLIOMA AND HIGH GRADE GLIOMA $1.8M 0 39
AN OPEN-LABEL, SAFETY STUDY FOR PREVIOUSLY TREATED VATIQUINONE (PTC743) SUBJECTS WITH INHERITED MITOCHONDRIAL DISEASE $1.7M 0 267
AN OPEN-LABEL TRIAL TO ADDRESS THE SAFETY OF THE SMARTFLOW MR COMPATIBLE VENTRICULAR CANNULA FOR ADMINISTERING ELADOCAGENE EXUPARVOVEC TO PEDIATRIC SUBJECTS $1.6M 3 33
A RANDOMIZED, PARALLEL-ARM, DOUBLE-BLIND, PLACEBO CONTROLLED STUDY WITH OPEN-LABEL EXTENSION TO ASSESS THE EFFICACY AND SAFETY OF VATIQUINONE FOR THE TREATMENT OF FRIEDREICH ATAXIA (MOVE-FA) $1.5M 2 183
A PHASE 1B STUDY OF UNESBULIN (PTC596) IN COMBINATION WITH DACARBAZINE IN PATIENTS WITH LOCALLY RECURRENT, UNRESECTABLE OR METASTATIC RELAPSED/REFRACTORY LEIOMYOSARCOMA $1.5M 0 92
PHASE 1B STUDY OF PTC299 IN RELAPSED/REFRACTORY ACUTE LEUKEMIAS $1.2M 0 155
AN OPEN-LABEL, SAFETY STUDY FOR PREVIOUSLY TREATED ATALUREN PATIENTS WITH NONSENSE MUTATION DYSTROPHINOPATHY $1.2M 0 248
PHASE 1 STUDY TO INVESTIGATE THE ABSORPTION, METABOLISM, AND EXCRETION OF 14C PTC923 FOLLOWING A SINGLE ORAL DOSE ADMINISTRATION IN HEALTHY MALE VOLUNTEERS $1.2M 0 10
PHASE 2 CLINICAL PHARMACOLOGY STUDY TO ASSESS DYSTROPHIN LEVELS IN SUBJECTS WITH NMDMD BEFORE AND AFTER TREATMENT WITH ATALUREN $1.1M 0 87
A PHASE 1 STUDY TO INVESTIGATE THE PHARMACOKINETICS OF PTC743 AND THE ABSORPTION, METABOLISM, AND EXCRETION OF 14C-PTC743 IN HEALTHY VOLUNTEERS $1.0M 0 9
A PHASE 3 STUDY OF PTC923 IN SUBJECTS WITH PHENYLKETONURIA $970,020 0 74
A RANDOMIZED, PARALLEL-ARM, DOUBLE-BLIND, PLACEBO CONTROLLED STUDY WITH OPEN-LABEL EXTENSION TO ASSESS THE EFFICACY AND SAFETY OF VATIQUINONE FOR THE TREATMENT OF FRIEDREICH ATAXIA $896,011 0 44
AN OPEN-LABEL, RANDOMIZED, SINGLE-DOSE, TWO-PERIOD CROSSOVER STUDY COMPARING THE BIOEQUIVALENCE OF DEFLAZACORT DISPERSIBLE TABLET TO EMFLAZA DEFLAZACORT TABLET IN HEALTHY ADULT SUBJECTS $869,415 0 8
A PHASE 1B STUDY OF PTC596 IN COMBINATION WITH DACARBAZINE IN PATIENTS WITH LOCALLY RECURRENT, UNRESECTABLE OR METASTATIC RELAPSED-REFRACTORY LEIOMYOSARCOMA $766,581 0 72
A PHASE 3 OPEN-LABEL STUDY OF PTC923 (SEPIAPTERIN) IN PHENYLKETONURIA $738,581 0 55
NELSON OBSERVATIONAL STUDY $733,501 0 7
Phase 1 open label single dos 4-group study to eveluate the PK and Safety of Ataluren in subjects with various severities of impaired Hepatic Function and healthy subjects $704,260 0 6
A PHASE 1, OPEN-LABEL STUDY TO INVESTIGATE THE ABSORPTION, METABOLISM, AND EXCRETION OF 14C-PTC518 IN HEALTHY MALE PARTICIPANTS $641,294 0 6
Open-Label, Safety Study for Previously Treated Ataluren (PTC124) Patients with Nonsense Mutation Dystrophinopathy in North America $570,036 0 84
LONG-TERM OPEN-LABEL STUDY TO ASSESS THE SAFETY AND EFFICACY OF VATIQUINONE IN PATIENTS WITH FRIEDREICH ATAXIA $527,481 0 120
A PHASE 2, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED, PARALLEL STUDY TO ASSESS THE EFFICACY, SAFETY, TOLERABILITY, PK, AND BIOMARKER EFFECTS OF PTC857 IN ADULT SUBJECTS WITH AMYOTROPHIC LATERAL SCLEROSIS (CARDINALS) $523,990 3 99
A PHASE 1 STUDY TO EVALUATE THE EFFECT OF HEPATIC IMPAIRMENT ON THE PHARMACOKINETICS OF SEPIAPTERIN $521,334 0 35
EVALUATING THE THERAPEUTIC POTENTIAL OF MAPT SPLICING MODULATIONIN HUMAN NEURONAL MODELS OF TAUOPATHY $475,400 0 4
A Phase 1 Study to investigate the absorption and metabolism of 14-C deflazacort following single oral dose administration in healthy subjects $416,003 0 9

Payments by Medical Specialty

Specialty Total Paid Doctors Avg/Doctor
Contractor $1.0M 1 $1.0M
Surgery $473,856 1 $473,856
Neurology with Special Qualifications in Child Neurology $452,513 198 $2,285
Neurology $241,076 127 $1,898
Clinical Genetics (M.D.) $234,486 33 $7,106
Pediatrics $230,538 232 $993.70
Student in an Organized Health Care Education/Training Program $166,332 38 $4,377
Pediatric Rehabilitation Medicine $111,483 12 $9,290
Clinical Biochemical Genetics $80,452 10 $8,045
Neuromuscular Medicine $59,399 21 $2,829
Neurological Surgery $56,778 12 $4,732
Neurodevelopmental Disabilities $54,110 21 $2,577
Internal Medicine $49,469 22 $2,249
Gastroenterology $46,309 6 $7,718
Pediatric Critical Care Medicine $44,808 1 $44,808
Hematology & Oncology $29,484 15 $1,966
Cardiovascular Disease $25,301 4 $6,325
Physical Medicine & Rehabilitation $23,282 30 $776.07
Pediatric Cardiology $19,296 14 $1,378
Medical Genetics, Ph.D. Medical Genetics $19,202 1 $19,202
Sleep Medicine $12,916 5 $2,583
Pediatric Pulmonology $12,846 12 $1,071
Vascular Neurology $11,656 5 $2,331
Nurse Practitioner $11,023 25 $440.93
Ophthalmology $10,325 6 $1,721
Child & Adolescent Psychiatry $9,684 4 $2,421
Pediatric Endocrinology $9,609 5 $1,922
Specialist $9,298 16 $581.11
Pediatric Anesthesiology $8,900 2 $4,450
Family $5,666 36 $157.38
Pediatric Gastroenterology $5,067 5 $1,013
Obstetrics & Gynecology $4,311 2 $2,156
Clinical Neurophysiology $4,118 5 $823.69
Clinical Pharmacology $3,924 1 $3,924
Health Maintenance Organization $3,616 1 $3,616
Medical Oncology $3,543 3 $1,181
Orthopaedic Surgery $3,364 4 $840.94
Neuromusculoskeletal Medicine & OMM $3,170 1 $3,170
Endocrinology, Diabetes & Metabolism $2,835 5 $567.09
Hematology $2,811 2 $1,405
Pediatric Infectious Diseases $2,800 1 $2,800
Registered Nurse $2,396 10 $239.60
Family Medicine $1,897 6 $316.19
Interventional Cardiology $1,891 1 $1,891
Medical $1,727 10 $172.69
Anesthesiology $1,576 3 $525.43
Anatomic Pathology $1,200 1 $1,200
Dermatology $1,112 2 $556.05
Physician Assistant $1,060 23 $46.07
Nephrology $1,000 1 $1,000
Nurse Anesthetist, Certified Registered $975.00 1 $975.00
Anatomic Pathology & Clinical Pathology $972.51 2 $486.26
Urology $940.52 1 $940.52
General Practice $590.11 5 $118.02
Epilepsy $523.69 8 $65.46
Electrodiagnostic Medicine $386.33 2 $193.17
Adolescent Medicine $334.67 3 $111.56
Medical Biochemical Genetics $292.00 5 $58.40
Public Health & General Preventive Medicine $281.25 1 $281.25
Pediatric Surgery $200.14 4 $50.04
Clinical Molecular Genetics $158.84 1 $158.84
Allergy $158.58 1 $158.58
Pain Medicine $145.13 1 $145.13
Primary Care $142.59 3 $47.53
Pediatric Orthopaedic Surgery $139.64 3 $46.55
Neurocritical Care $134.04 2 $67.02
Clinical Cytogenetics $128.75 1 $128.75
Neonatal-Perinatal Medicine $128.59 1 $128.59
Psychiatric/Mental Health $125.00 1 $125.00
Psychiatry $112.46 4 $28.12
Radiation Oncology $107.31 1 $107.31
Advanced Practice Midwife $62.89 1 $62.89
Maternal & Fetal Medicine $62.81 1 $62.81
Genetic Counselor, MS $60.15 1 $60.15
Pulmonary Disease $56.69 2 $28.35
Interventional Pain Medicine $39.02 1 $39.02
Neonatal Intensive Care $37.36 1 $37.36
Developmental - Behavioral Pediatrics $36.87 2 $18.44
Emergency Medicine $34.82 2 $17.41
Brain Injury Medicine $33.54 1 $33.54
Advanced Heart Failure and Transplant Cardiology $31.53 1 $31.53
Athletic Trainer $27.34 1 $27.34
Pediatric Hematology-Oncology $24.17 1 $24.17
Surgical $24.17 1 $24.17
Pediatric Rheumatology $23.00 1 $23.00
Neuroradiology $16.24 1 $16.24
Neuromusculoskeletal Medicine, Sports Medicine $14.58 1 $14.58
Hospitalist $13.34 1 $13.34
Retina Specialist $12.57 1 $12.57

Top Paid Doctors — Page 2

Doctor Specialty Location Total 2023
Dr. Migvis Monduy, M.d, M.D Neurology with Special Qualifications in Child Neurology Miami, FL $23,546 $0
Oscar Mayer, M.d, M.D Pediatrics Philadelphia, PA $22,683 $0
Dr. Paldeep Atwal, Md, MD Clinical Genetics (M.D.) West Palm Beach, FL $22,583 $0
Phillip Pearl, Md, MD Neurology with Special Qualifications in Child Neurology Boston, MA $22,208 $0
Dr. Roberto Zori, Md, MD Clinical Genetics (M.D.) Gainesville, FL $21,037 $0
John Osborne, Md, MD Cardiovascular Disease Grapevine, TX $20,713 $0
Kevin Flanigan, Md, MD Neurology with Special Qualifications in Child Neurology Columbus, OH $20,145 $0
Vamshi Rao, Md, MD Neurology with Special Qualifications in Child Neurology Chicago, IL $19,430 $0
Dr. Gerard Vockley, Md, Phd, MD, PHD Medical Genetics, Ph.D. Medical Genetics Pittsburgh, PA $19,202 $0
Dr. Clifton Gooch, M.d, M.D Neurology Tampa, FL $18,563 $0
Dr. Richard Bedlack, M.d. Ph.d, M.D. PH.D Neurology Durham, NC $18,140 $0
William Burnette, Md, MD Neuromuscular Medicine Nashville, TN $18,093 $0
Andres Gelrud, M.d, M.D Gastroenterology Miami, FL $17,500 $0
Dr. Horacio Kaufmann, M.d, M.D Neurology New York, NY $17,071 $0
Farida Abid, Md, MD Neurology with Special Qualifications in Child Neurology Houston, TX $16,836 $0
Dr. Joseph Ray, M.d, M.D Clinical Genetics (M.D.) Galveston, TX $16,333 $0
Dr. Robert Enelow, M.d, M.D Internal Medicine Washington, DC $15,572 $0
Erin Furr Stimming, M.d, M.D Neurology Houston, TX $13,481 $0
Dr. Paul Watkins, Md, MD Gastroenterology Chapel Hill, NC $13,125 $0
Dr. Barry Byrne, Md, MD Pediatric Cardiology Gainesville, FL $11,812 $0
Andrew Siderowf, Md, MD Neurology Philadelphia, PA $11,635 $0
Daniel Curry, Md, MD Neurological Surgery Houston, TX $11,613 $0
Perry Shieh, Md, MD Neuromuscular Medicine Los Angeles, CA $11,456 $0
Dr. Claudia Chiriboga, M.d, M.D Neurology with Special Qualifications in Child Neurology New York, NY $11,452 $0
Dr. Stephen Cederbaum, M.d, M.D Clinical Genetics (M.D.) Los Angeles, CA $11,304 $0

Top Products

  • EMFLAZA $1.3M
  • Emflaza $596,188

Associated Products (2)

Payment Categories

  • Food & Beverage $98,485
  • Consulting $2.8M
  • Travel & Lodging $294,283
  • Research $49.2M
  • Royalties $482,303

About PTC Therapeutics, Inc.

PTC Therapeutics, Inc. has made $56.6M in payments to 1,083 healthcare providers, recorded across 9,790 transactions in the CMS Open Payments database. In 2024, the company paid $8.4M. The top product by payment volume is EMFLAZA ($1.3M).

Payments were distributed across 89 medical specialties. The top specialty by payment amount is Contractor ($1.0M to 1 doctors).

Payment categories include: Food & Beverage ($98,485), Consulting ($2.8M), Research ($49.2M), Travel & Lodging ($294,283), Royalties ($482,303).

PTC Therapeutics, Inc. is associated with 2 products in the CMS Open Payments database.